Subjects: *AMYOTROPHIC lateral sclerosis; *CLINICAL trials; *GENE therapyITALY
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Subjects: *MUSCULAR dystrophy treatment; *GENETIC disorder treatment; *ORGANIZATIONAL transparencyITALYTELETHON (Organization)
Subjects: *CONFERENCES & conventions; *VIROLOGY; *SCIENTISTSORVIETO (Italy); ITALY
Subjects: *STEM cell treatment; *METACHROMATIC leukodystrophy; *LEUKODYSTROPHYITALY