Subjects: *GENE therapy; *DELPHI method; *HEMOPHILIAITALY
Record details
Subjects: *GENE therapy; *BISPECIFIC antibodies; *HEMOPHILIACSITALY
Subjects: *GENE therapy; *RETINAL diseases; *GENETIC disordersITALY
Subjects: *GENE therapy; *HEMATOPOIETIC stem cells; *GENETIC transformationITALY; UNITED States
Subjects: *GENE therapy; *CONFERENCES & conventionsITALY; ROME (Italy)
Subjects: *CONFERENCES & conventions; *CELLULAR therapy; *GENE therapyMILAN (Italy); ITALY
Subjects: *GENETIC engineering; *GENE therapy; *PHOSPHOLIPIDSITALY
Subjects: *TREATMENT of spinal muscular atrophy; *INTRAVENOUS therapy; *HEALTH status indicatorsITALY
Subjects: *CHARITIES; *RESEARCH institutes; *GENETIC disordersITALY
Subjects: *GLYCOGEN storage disease type II; *MONONUCLEAR leukocytes; *GENE therapyMILAN (Italy); ITALYGLAXOSMITHKLINE
Subjects: *AMYOTROPHIC lateral sclerosis; *CLINICAL trials; *GENE therapyITALY
Subjects: *MUSCULAR dystrophy treatment; *GENETIC disorder treatment; *ORGANIZATIONAL transparencyITALYTELETHON (Organization)
Subjects: *CONFERENCES & conventions; *VIROLOGY; *SCIENTISTSORVIETO (Italy); ITALY
Subjects: *STEM cell treatment; *METACHROMATIC leukodystrophy; *LEUKODYSTROPHYITALY