Item request has been placed!
×
Item request cannot be made.
×
Processing Request
Item request has been placed!
×
Item request cannot be made.
×
Processing Request
Subjects: Orphan Drug Production* ; Drug Approval*; United States
-
Source:
The Milbank quarterly [Milbank Q] 2024 Mar; Vol. 102 (1), pp. 83-96. Date of Electronic Publication: 2023 Dec 12.Publisher: Blackwell Publishers Country of Publication: United States NLM ID: 8607003 Publication Model: Print-Electronic Cited Medium: Internet
Record details
-
Authors :
Bouwman L; Faculdade de Farmácia, Universidade de Lisboa, Lisbon, Portugal. .; Laboratory of Systems Integration Pharmacology, Clinical and Regulatory Science, Research Institute for Medicines of the University of Lisbon (iMED.ULisboa), Lisbon, Portugal. .
Subjects: Orphan Drug Production* ; Rare Diseases*/Rare Diseases*/Rare Diseases*/drug therapy; Humans
-
Source:
Orphanet journal of rare diseases [Orphanet J Rare Dis] 2024 Feb 27; Vol. 19 (1), pp. 91. Date of Electronic Publication: 2024 Feb 27.Publisher: BioMed Central Country of Publication: England NLM ID: 101266602 Publication Model: Electronic Cited Medium: Internet ISSN: 1750-1172
Record details
-
Authors :
Belot A; Centre International de Recherche en Infectiologie, Inserm U1111, Université Claude Bernard Lyon 1, CNRS UMR5308, ENS de Lyon, Lyon, France; Pediatric Nephrology, Rheumatology, Dermatology, Hôpital Femme Mère Enfant, Hospices Civils de Lyon, Bron 69677, France. Electronic address: .
Subjects: Rare Diseases*/Rare Diseases*/Rare Diseases*/drug therapy ; Orphan Drug Production*; Humans
-
Source:
Lancet (London, England) [Lancet] 2024 Feb 17; Vol. 403 (10427), pp. 592-593. Date of Electronic Publication: 2024 Jan 23.Publisher: Elsevier Country of Publication: England NLM ID: 2985213R Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1474-547X
Record details
-
Authors :
Seoane-Vazquez E; Department of Pharmaceutical Economic and Policy, Chapman University School of Pharmacy, Irvine, CA, USA. .; Economic Science Institute, Argyros School of Business and Economics, Chapman University, Orange, CA, USA. .
Subjects: Orphan Drug Production* ; Biological Products*/Biological Products*/Biological Products*/therapeutic use; United States
-
Source:
Scientific reports [Sci Rep] 2024 Feb 09; Vol. 14 (1), pp. 3325. Date of Electronic Publication: 2024 Feb 09.Publisher: Nature Publishing Group Country of Publication: England NLM ID: 101563288 Publication Model: Electronic Cited Medium: Internet ISSN:
Record details
Subjects: Orphan Drug Production*; Humans ; India
-
Source:
Journal of biosciences [J Biosci] 2024; Vol. 49.Publisher: Springer India, in co-publication with Indian Academy of Sciences Country of Publication: India NLM ID: 8100809 Publication Model: Print Cited
Record details
-
Authors :
Vogel M; John F. Kennedy School of Government, Harvard University, Cambridge, Massachusetts.; Zhao O
Subjects: Medicare* ; Orphan Drug Production*; Humans
-
Source:
JAMA internal medicine [JAMA Intern Med] 2024 Jan 01; Vol. 184 (1), pp. 63-69.Publisher: American Medical Association Country of Publication: United States NLM ID: 101589534 Publication Model: Print Cited Medium: Internet ISSN:
Record details
-
Authors :
Costa E; WHO Collaborating Centre for Pharmaceutical Policy and Regulation, Department of Pharmacoepidemiology, Utrecht University, Utrecht, Kingdom of the Netherlands.; Moja L
Subjects: Orphan Drug Production* ; Drugs, Essential*; Child
-
Source:
Bulletin of the World Health Organization [Bull World Health Organ] 2024 Jan 01; Vol. 102 (1), pp. 22-31. Date of Electronic Publication: 2023 Oct 31.Publisher: World Health Organization Country of Publication: Switzerland NLM ID: 7507052 Publication Model: Print-Electronic Cited Medium: Internet
Record details
-
Authors :
Palomo GM; Agencia Española de Medicamentos y Productos Sanitarios, Calle Campezo 1 Edificio 8, 28022 Madrid, Spain; Committee for Orphan Medicinal Products, European Medicines Agency, Domenico Scarlattilaan 6, 1083 HS Amsterdam, the Netherlands. Electronic address: .
Subjects: Rare Diseases*/Rare Diseases*/Rare Diseases*/genetics ; Rare Diseases*/Rare Diseases*/Rare Diseases*/therapy ; Orphan Drug Production*
-
Source:
Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2023 Dec 06; Vol. 31 (12), pp. 3414-3423. Date of Electronic Publication: 2023 Oct 04.Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN:
Record details
-
Authors :
Williamson J; Faron Pharmaceuticals, Joukahaisenkatu 6, 20520 Turku, Finland. Electronic address: .; Spicer AJ
Subjects: Orphan Drug Production* ; Drug Approval*; United States
-
Source:
Drug discovery today [Drug Discov Today] 2023 Dec; Vol. 28 (12), pp. 103807. Date of Electronic Publication: 2023 Oct Publisher: Elsevier Science Ltd. Country of Publication: England NLM ID: 9604391 Publication Model: Print-Electronic Cited Medium: Internet ISSN:
Record details
