Subjects: GENE therapy; PATIENT safety; DRUG administration
Record details
Subjects: MORTALITY risk factors; GENE therapy; COMBINATION drug therapy
Subjects: SPINAL muscular atrophy; RETROSPECTIVE studies; SEVERITY of illness index
Subjects: TREATMENT of Duchenne muscular dystrophy; STATISTICS; ANALYSIS of variance
Subjects: TREATMENT of spinal muscular atrophy; ONLINE information services; SYSTEMATIC reviews