Search Results

Effect of etranacogene dezaparvovec on quality of life for severe and moderately severe haemophilia B participants: Results from the phase III HOPE‐B trial 2 years after gene therapy.

• Authors : Itzler, Robbin; Buckner, Tyler W.; Leebeek, Frank W. G.

Subjects: CLINICAL trials; GENE therapy; BLOOD coagulation factor IX

• Source: Haemophilia; May2024, Vol. 30 Issue 3, p709-719, 11p

Record details

Riboswitch-controlled IL-12 gene therapy reduces hepatocellular cancer in mice.

• Authors : Düchs, Matthias J.; Kratzer, Ramona F.; Vieyra-Garcia, Pablo

Subjects: HEPATOCELLULAR carcinoma; LIVER cancer; GENE therapy

• Source: Frontiers in Immunology; 2024, p1-19, 19p

Record details

Safety and Efficacy of IL-12 Plasmid DNA Transfection into Pig Skin: Supportive Data for Human Clinical Trials on Gene Therapy and Vaccination.

• Authors : Lampreht Tratar, Ursa; Jesenko, Tanja; Omerzel, Masa

Subjects: GENE therapy; CLINICAL trials; DNA vaccines

• Source: International Journal of Molecular Sciences; Mar2024, Vol. 25 Issue 6, p3151, 12p

Record details

Recent developments in gene therapy research in India.

• Authors : Selot, Ruchita; Ghosh, Arkasubhra

• Source: Journal of Biosciences; Mar2024, Vol. 49 Issue 1, p1-26, 26p

Record details

Gene Therapy for Genetic Syndromes: Understanding the Current State to Guide Future Care.

• Authors : Henderson, Marian L.; Zieba, Jacob K.; Li, Xiaopeng

Subjects: GENE therapy; SPINAL muscular atrophy; DUCHENNE muscular dystrophy

• Source: BioTech; Mar2024, Vol. 13 Issue 1, p1, 31p

Record details

Gene therapy for adenosine deaminase severe combined immune deficiency—An unexpected journey of four decades.

• Authors : Kohn, Donald B.

Subjects: ADENOSINE deaminase; GENE therapy; IMMUNODEFICIENCYEUROPEAN Union; EUROPEAN Medicines Agency

• Source: Immunological Reviews; Mar2024, Vol. 322 Issue 1, p148-156, 9p

Record details

Navigating Gene Therapy Access: The Case of Bulgaria in the Context of the EU Regulatory Landscape.

• Authors : Kostadinov, Kostadin; Marinova, Yuliyana; Dimitrov, Kostadin

Subjects: HEALTH services accessibility; RESEARCH methodology; UNCERTAINTYBULGARIAEUROPEAN Union

• Source: Healthcare (2227-9032); Feb2024, Vol. 12 Issue 4, p458, 13p

Record details

AAV-RPGR Gene Therapy Rescues Opsin Mislocalisation in a Human Retinal Organoid Model of RPGR -Associated X-Linked Retinitis Pigmentosa.

• Authors : Sladen, Paul E.; Naeem, Arifa; Adefila-Ideozu, Toyin

Subjects: RETINITIS pigmentosa; GENE therapy; CLINICAL trials

• Source: International Journal of Molecular Sciences; Feb2024, Vol. 25 Issue 3, p1839, 14p

Record details

An Overview of the use of Gene Therapy in Cancer Treatment.

• Authors : Islam Sk, Md Safiqul; Sharma, Taniya; Tiwari, Himani

Subjects: GENE therapy; CANCER treatment; CANCER genes

• Source: International Journal of Pharmacy & Life Sciences; Jan2024, Vol. 15 Issue 1, p30-41, 12p

Record details

Gene therapy for glycogen storage diseases.

• Authors : Koeberl, Dwight D.; Koch, Rebecca L.; Lim, Jeong‐A.

• Source: Journal of Inherited Metabolic Disease; Jan2024, Vol. 47 Issue 1, p93-118, 26p

Record details