Subjects: *HEALTH facilities; GENE therapy; SPOKESPERSONSBIOMARIN Pharmaceutical Inc. BIOMARIN Pharmaceutical Inc. BIOMARIN Pharmaceutical Inc. BMRN
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Subjects: GENE therapy; MUSCLE diseases; CARDIAC patientsPFIZER Inc. 001326495 PFIZER Inc. PFIZER Inc. 001326495 001326495 PFIZER Inc. 001326495 PFE
Subjects: GENE therapy; HEMOPHILIACS; BLOOD coagulation factor IXPFIZER Inc. 001326495 PFIZER Inc. PFIZER Inc. 001326495 001326495 PFIZER Inc. 001326495 PFE
Subjects: *PRICES; GENE therapy; DRUG abuse prevention
Subjects: GENE therapy; CRISPRS; SICKLE cell anemia
Subjects: GENE therapy; MUSCLE diseases; DUCHENNE muscular dystrophy
Subjects: *FINANCIAL stress; GENE therapy; SICKLE cell anemiaUNITED States. Food & Drug Administration
Subjects: *VALUE investing (Finance); GENE therapy; SICKLE cell anemiaUNITED States. Food & Drug Administration ; VERTEX Pharmaceuticals Inc. 602478257 VERTEX Pharmaceuticals Inc. VERTEX Pharmaceuticals Inc. 602478257 602478257 VERTEX Pharmaceuticals Inc. 602478257 VRTX
Subjects: GENE therapy; LIVER diseases; RARE diseases